ITINERARE Symposium 2022

14:00 - 14:10

Welcome
speech

  Opening

  Prof. Janine Reichenbach (Director ITINERARE)
  Institute for Regenerative Medicine (IREM), University of Zurich

  Prof. Elisabeth Stark
  Vice President Research, University of Zurich

Chair              

  Prof. Olivier Devuyst (Co-director ITINERARE)
  Institute of Physiology, University of Zurich

14:10 - 14:40

  Gene therapies for rare disease: development and access
  challenges from a Primary Immunodeficiency perspective

  Leire Solis
  International Patient Organisation for Primary
  Immunodeficiencies, (IPOPI), UK

14:40 - 15:10

  Advances in the gene therapy of blood cell diseases

  Dr. Juan Bueren

  CIEMAT Group Hematopoietic innovative therapies, Spain

  Presentation Bueren

15:10 - 15:40

  From genetic to auto-immune predisposition to life- 

  threatening COVID 19

  Dr. Paul Bastard
  Imagine Institute Paris, France

  Presentation Bastard

15:40 - 16:10

  Coffee Break

Chair

  Prof. Matthias Baumgartner (Co-director ITINERARE)

  Division of Metabolic Diseases, University Children's Hospital
  Zurich

16:10 - 16:40

  Access and development of orphan drugs: the role of
  academia

  Prof. Carla Hollak
  University Medical Center Amsterdam, The Netherlands

  Presentation Hollak

16:40 - 17:00

  Hopes, Privileges and Money – Orphan Drug Pricing in Germany

  Dr. Thomas Kapitza
  M&E Ethics Lab, IBME, University of Zurich

17:00 - 17:45

Panelists

Moderation

  Panel Discussion

  - Innovative therapies for rare diseases: what are fair prices? -
  Dr. Ursula Schafroth
  SGV, Switzerland
  Prof. Michael Coors
  Institute of Social Ethics,University of Zurich
  Shayesteh Fürst-Ladani
  Rare Disease  Action Forum (RDAF), Switzerland
  Prof. Nikola Biller-Andorno (Deputy Director ITINERARE)
  IBME, University of Zurich

Ab 17:45

  Networking Apéro