Sitemap URPP ITINERARE About us Organization Advisory Board Steering Committee Directorate Researchers Management Office Research Gene editing, Targeting and Delivery Urea cycle disorders Myeloid targeted gene therapy Primary aldosteronism Childhood dementia Molecular Therapies LoF mutations - Methylmalonic aciduria LoF mutations - Dent and Lowe syndrome GoF mutations - Epileptic encephalopathy GoF mutations - Tubulointersitial kidney disease Social Innovations Legal and policy aspects Ethical and psychosocial aspects ITINERARE Junior Grants Research project on Vanishing White Matter Disease Research project on Remethylation Disorders Research project on rare endolysosomal disorders Research project on stakeholders in rare disease health care Publications Education and Training Programs Events ITINERARE Symposium ITINERARE Symposium 2021 Rare Disease Summer School 8th Rare Disease Summer School radiz Summer School (2013-2019) 1st Rare Disease Summer School 2nd Rare Disease Summer School 3rd Rare Disease Summer School 4th Rare Disease Summer School 5th Rare Disease Summer School 6th Rare Disease Summer School 7th Rare Disease Summer School News